🇺🇸 FDA
Pipeline program

Phenoptin

PKU-007

Phase 2 small_molecule completed

Quick answer

Phenoptin for Tetrahydrobiopterin Deficiencies is a Phase 2 program (small_molecule) at BioMarin International Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
BioMarin International Limited
Indication
Tetrahydrobiopterin Deficiencies
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials