Friday, July 10, 2026

pharma · Phenylketonuria · Achondroplasia

BioMarin Pharmaceutical Australia

BioMarin Pharmaceutical Australia is a pharma organization headquartered in San Rafael, USA. Primary therapeutic focus areas include Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hy

770 Lindaro Street, San Rafael, CA 94901, US HQ
1997 Founded
3,171 Employees
TGA registrant Type
Company details
Status
Public
HQ
770 Lindaro Street, San Rafael, CA 94901, US
Founded
1997
Employees
3,171
Programs
91
Drugs
36
Patents
175
Clinical program

PARP inhibitor BMN-673

Phase 1 · small molecule · Metastatic Cancer

PARP inhibitor BMN-673 for Metastatic Cancer is a Phase 1 program (small_molecule) at BioMarin Pharmaceutical Australia Pty Ltd with 1 ClinicalTrials.gov record(s).

Internal code 13-001857

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
BioMarin Pharmaceutical Australia Pty Ltd
Phase
Phase 1
Modality
small_molecule
Indication
Metastatic Cancer
Status
completed
Trials
1

Clinical trials