🇺🇸 FDA
Pipeline program

N-acetylgalactosamine 4-sulfatase

ASB-01-04

Phase 3 small_molecule completed

Quick answer

N-acetylgalactosamine 4-sulfatase for Mucopolysaccharidosis VI is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 3 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Mucopolysaccharidosis VI
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials