🇺🇸 FDA
Pipeline program

Drisapersen

DMD115501

Phase 3 small_molecule terminated

Quick answer

Drisapersen for Muscular Dystrophies is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 2 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Muscular Dystrophies
Phase
Phase 3
Modality
small_molecule
Status
terminated

Clinical trials