🇺🇸 FDA
Pipeline program

BMN 701

POM-001

Phase 2 mab completed

Quick answer

BMN 701 for Pompe Disease is a Phase 2 program (mab) at BioMarin International Limited with 2 ClinicalTrials.gov record(s).

Program details

Company
BioMarin International Limited
Indication
Pompe Disease
Phase
Phase 2
Modality
mab
Status
completed

Clinical trials