🇺🇸 FDA
Pipeline program

BMN 349

349-102

Phase 1 small_molecule active

Quick answer

BMN 349 for Alpha 1-Antitrypsin Deficiency is a Phase 1 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Alpha 1-Antitrypsin Deficiency
Phase
Phase 1
Modality
small_molecule
Status
active

Clinical trials