Exon 51 specific phosphorothioate oligonucleotide
351-202
Phase 2 small_molecule active
Quick answer
Exon 51 specific phosphorothioate oligonucleotide for Duchenne Muscular Dystrophy is a Phase 2 program (small_molecule) at BioMarin International Limited with 1 ClinicalTrials.gov record(s).
Program details
- Company
- BioMarin International Limited
- Indication
- Duchenne Muscular Dystrophy
- Phase
- Phase 2
- Modality
- small_molecule
- Status
- active