Wednesday, June 10, 2026

pharma Β· Growth Hormone Deficiency, Pediatric

Ascendis Pharma

Ascendis Pharma drug portfolio β€” 7 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Palo Alto, USA HQ
2010 Founded
5 Employees
EMA registrant Type
Company details
Status
Public
HQ
Palo Alto, USA
Founded
2010
Employees
5
Programs
2
Drugs
7
Patents
6
Intelligence Β· Drug Pipeline

Ascendis Pharma pipeline

Portfolio lens on 7 drugs and development assets β€” regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Ascendis Pharma drug portfolio β€” 7 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

7 compounds
  1. US regulatory status: approved. Mechanism: Dihydrofolate reductase inhibitor.

    Mechanism
    Dihydrofolate reductase inhibitor
  2. US regulatory status: approved. Mechanism: Unknown.

    Mechanism
    Unknown
  3. US regulatory status: approved. Molecular target: Bacterial 70S ribosome.

    Target
    Bacterial 70S ribosome
    Mechanism
    Bacterial 70S ribosome inhibitor
  4. Development asset linked to Ascendis Pharma in public FDA and regional records.

  5. lonapegsomatropin

    Systemic hormonal preparations (H01)

    Systemic hormonal preparations (H01) compound in Ascendis Pharma's portfolio. Molecular target: Growth hormone receptor.

    Target
    Growth hormone receptor
    Mechanism
    Growth hormone receptor agonist
  6. somatropin

    Systemic hormonal preparations (H01)

    US regulatory status: approved. Molecular target: Growth hormone receptor.

    Target
    Growth hormone receptor
    Mechanism
    Growth hormone receptor agonist
  7. Development asset linked to Ascendis Pharma in public FDA and regional records.