🇺🇸 FDA
Pipeline program

givosiran (ALN-AS1)

ALN-AS1-001

Phase 1 small_molecule completed

Quick answer

givosiran (ALN-AS1) for Acute Intermittent Porphyria is a Phase 1 program (small_molecule) at Alnylam Netherlands B.V. with 1 ClinicalTrials.gov record(s).

Program details

Company
Alnylam Netherlands B.V.
Indication
Acute Intermittent Porphyria
Phase
Phase 1
Modality
small_molecule
Status
completed

Clinical trials