Company profile · Sponsor
Alnylam
Alnylam Netherlands B.V.
- Pipeline
- 24
- Drugs
- 8
- Patents
- 8
Quick answer
Alnylam (ALNY) is a pharma company. headquartered in CAMBRIDGE, MA, EU. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 8 drugs, and 8 patents to this profile..
Company facts
Pipeline (24)
Search pipeline →-
0.9% (w/v) sodium chloride with 5 mM phosphate buffered solution, Zilebesiran
Alnylam
High cardiovascular risk, Established cardiovascular disease, Hypertension
1 trial -
0.9% Sodium chloride, Amvuttra 25 mg solution for injection in pre-filled syringe
Alnylam
Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)
1 trial -
ALN-TTRSC04, Amvuttra 25 mg solution for injection in pre-filled syringe
Alnylam
Hereditary transthyretin-mediated amyloidosis with polyneuropathy
1 trial -
Amvuttra 25 mg solution for injection in pre-filled syringe
Alnylam
Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)
1 trial -
Amvuttra 25 mg solution for injection in pre-filled syringe, Onpattro 2 mg/mL concentrate for solution for infusion.
Alnylam
Hereditary Transthyretin Amyloidosis
1 trial -
Givosiran
Alnylam
Acute Hepatic Porphyria
1 trial -
Lumasiran
Alnylam
Primary Hyperoxaluria Type 1
1 trial -
Lumasiran
Alnylam
Primary Hyperoxaluria
1 trial -
Nucresiran
Alnylam
Transthyretin Amyloidosis With Cardiomyopathy
1 trial -
Nucresiran
Alnylam
Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy
1 trial -
Onpattro 2 mg/mL concentrate for solution for infusion., Sodium Chloride Intravenous Infusion BP 0.9% w/v
Alnylam
Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)
1 trial -
Patisiran
Alnylam
Amyloidosis
1 trial -
Patisiran
Alnylam
Amyloidosis, Familial
1 trial -
Patisiran
Alnylam
Amyloidosis, Hereditary
1 trial -
Placebo
Alnylam
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
1 trial -
Placebo
Alnylam
Primary Hyperoxaluria Type 1 (PH1)
1 trial -
Placebo for Nucresiran, ALN-TTRSC04
Alnylam
Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with Cardiomyopathy)
1 trial -
Revusiran (ALN-TTRSC)
Alnylam
Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
1 trial -
Vutrisiran
Alnylam
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
2 trials -
Zilebesiran
Alnylam
High Risk Cardiovascular Disease
1 trial -
patisiran (ALN-TTR02)
Alnylam
TTR-mediated Amyloidosis
1 trial -
ALN-2232
Alnylam
Obesity
1 trial -
ALN-4324
Alnylam
Type 2 Diabetes Mellitus (T2DM)
1 trial -
ALN-4324
Alnylam
Obese or Overweight Healthy Volunteers
1 trial
Drugs (8)
Search drugs →Patents (8)
Search patents →-
US 12416006
Cell death-inducing DFFA-like effector B (CIDEB) iRNA compositions and methods of use thereof
granted -
US 12404508
Ketohexokinase (KHK) iRNA compositions and methods of use thereof
granted -
US 12397013
Extrahepatic delivery
granted -
US 12385044
Modified double-stranded RNA agents
granted -
US 12385043
Modified double-stranded RNA agents
granted -
US 12378553
Modified double-stranded RNA agents
granted -
US 12364762
Biodegradable lipids for the delivery of active agents
granted -
US 12350338
Biodegradable lipids for the delivery of active agents
granted
Frequently asked questions
What is Alnylam?
Alnylam (ALNY) is a pharma company. headquartered in CAMBRIDGE, MA, EU. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 8 drugs, and 8 patents to this profile..
What pipeline programs does Alnylam sponsor?
We track 24 ClinicalTrials.gov-linked programs for Alnylam, including 0.9% (w/v) sodium chloride with 5 mM phosphate buffered solution, Zilebesiran and 23 more. Open each program for phase, modality, NCT IDs, and indication details.
Where does Alnylam company data come from?
Profiles combine SEC EDGAR (CIK/ticker), ClinicalTrials.gov sponsor links, FDA drug records, and USPTO patent metadata. See our data sources page. This profile is for professional reference, not investment advice.