🇺🇸 FDA
Pipeline program

Givosiran

ALN-AS1-003

Phase 3 small_molecule completed

Quick answer

Givosiran for Acute Hepatic Porphyria is a Phase 3 program (small_molecule) at Alnylam Netherlands B.V. with 1 ClinicalTrials.gov record(s).

Program details

Company
Alnylam Netherlands B.V.
Indication
Acute Hepatic Porphyria
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials