🇺🇸 FDA
Pipeline program

Mitapivat

AG348-C-025

Approved small_molecule active

Quick answer

Mitapivat for Pyruvate Kinase Deficiency is a Approved program (small_molecule) at Agios Netherlands B.V. with 2 ClinicalTrials.gov record(s).

Program details

Company
Agios Netherlands B.V.
Indication
Pyruvate Kinase Deficiency
Phase
Approved
Modality
small_molecule
Status
active

Clinical trials