Wednesday, June 10, 2026

pharma Β· Pyruvate Kinase Deficiency Β· Sickle Cell Disease Β· AGIO

Agios Netherlands

Agios Netherlands drug portfolio β€” 15 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

CAMBRIDGE, MA, NL HQ
1978 Founded
20 Employees
Public company Type
AGIO Β· NYSE Ticker
Company details
Status
Public
HQ
CAMBRIDGE, MA, NL
Founded
1978
Employees
20
Programs
45
Drugs
15
Patents
93
Intelligence Β· Drug Pipeline

Agios Netherlands pipeline

Portfolio lens on 15 drugs and development assets β€” regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Agios Netherlands drug portfolio β€” 15 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

15 compounds
  1. US regulatory status: approved. Molecular target: Isocitrate dehydrogenase [NADP], mitochondrial.

    Target
    Isocitrate dehydrogenase [NADP], mitochondrial
    Mechanism
    Isocitrate dehydrogenase [NADP], mitochondrial inhibitor
  2. Development asset linked to Agios Netherlands in public FDA and regional records.

  3. Development asset linked to Agios Netherlands in public FDA and regional records.

  4. US regulatory status: approved. Molecular target: Lanosterol 14-alpha demethylase.

    Target
    Lanosterol 14-alpha demethylase
    Mechanism
    Cytochrome P450 51 inhibitor
  5. ivosidenib

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: Isocitrate dehydrogenase [NADP] cytoplasmic.

    Target
    Isocitrate dehydrogenase [NADP] cytoplasmic
    Mechanism
    Isocitrate dehydrogenase [NADP] cytoplasmic inhibitor
  6. Development asset linked to Agios Netherlands in public FDA and regional records.

  7. mitapivat

    Blood and blood forming organs (B06)

    Blood and blood forming organs (B06) compound in Agios Netherlands's portfolio. Molecular target: Pyruvate kinase PKLR.

    Target
    Pyruvate kinase PKLR
    Mechanism
    Pyruvate kinase isozymes R/L activator
  8. US regulatory status: approved. Molecular target: Pyruvate kinase PKLR.

    Target
    Pyruvate kinase PKLR
    Mechanism
    Pyruvate kinase isozymes R/L activator
  9. nivolumab

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: Programmed cell death protein 1.

    Target
    Programmed cell death protein 1
    Mechanism
    Programmed cell death protein 1 inhibitor
  10. US regulatory status: approved. Molecular target: Copper.

    Target
    Copper
    Mechanism
    Copper chelating agent
  11. Development asset linked to Agios Netherlands in public FDA and regional records.

  12. Development asset linked to Agios Netherlands in public FDA and regional records.

  13. Development asset linked to Agios Netherlands in public FDA and regional records.

  14. Development asset linked to Agios Netherlands in public FDA and regional records.

  15. Development asset linked to Agios Netherlands in public FDA and regional records.