Friday, July 10, 2026

Drug profile · INN

vutrisiran

vutrisiran (AMVUTTRA) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.

EMA: approved TGA: approved Nervous system (N07) N07XX18
Patents linked 0
Pipeline programs 5
News articles 1
Drug details — vutrisiran

Quick answer

vutrisiran (AMVUTTRA) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.

Key facts

INN vutrisiran
Brand AMVUTTRA
Mechanism Transthyretin mRNA rnai inhibitor
Target Transthyretin mRNA
Therapeutic class Nervous system (N07)
ATC code N07XX18

Mechanism of action

Transthyretin mRNA rnai inhibitor

Primary target: Transthyretin mRNA

Approval history

Authority Status Date
EMA approved
TGA approved

Recent coverage

Pipeline programs

  1. ALN-TTRSC02-002 Phase 3 · Alnylam Netherlands · Hereditary Transthyretin Amyloidosis
  2. ALN-TTRSC02-003 Phase 3 · Alnylam Netherlands · Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloido
  3. ALN-TTRSC04-004 Phase 3 · Alnylam Netherlands · Hereditary transthyretin-mediated amyloidosis with polyneuro
  4. Amvuttra 25 mg solution for injection in pre-filled syringe Phase 3 · Alnylam Netherlands · Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloido
  5. Vutrisiran Phase 3 · Alnylam Netherlands · Transthyretin Amyloidosis (ATTR) With Cardiomyopathy

Related & competitor drugs

  1. aripiprazole Nervous system (N05)
  2. brexpiprazole Nervous system (N05)
  3. brivaracetam Nervous system (N03)
  4. bupivacaine Nervous system (N01)
  5. buprenorphine Nervous system (N07)
  6. caffeine citrate Nervous system (N06)

Frequently asked questions

What is vutrisiran?

vutrisiran (AMVUTTRA) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.

What is the brand name for vutrisiran?

AMVUTTRA is a marketed brand name for vutrisiran. Check FDA Drugs@FDA for the current US label holder and prescribing information.