Drug profile · INN
patisiran
ONPATTRO
patisiran (ONPATTRO) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.
Drug details — patisiran
- Class
- Nervous system (N07)
- Route
- —
- Patents
- 0
- Programs
- 10
- Data quality
- 0.89
Quick answer
patisiran (ONPATTRO) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.
Key facts
Mechanism of action
Transthyretin mRNA RNAi inhibitor
Primary target: Transthyretin mRNA
Approval history
| Authority | Status | Date |
|---|---|---|
| EMA | approved | — |
| TGA | approved | — |
Pipeline programs
Related & competitor drugs
Frequently asked questions
What is patisiran?
patisiran (ONPATTRO) is a transthyretin mrna rnai inhibitor. Associated with Lacuna Pharma Pty Ltd.
What is the brand name for patisiran?
ONPATTRO is a marketed brand name for patisiran. Check FDA Drugs@FDA for the current US label holder and prescribing information.