Friday, July 10, 2026

Drug profile · INN

olipudase alfa

olipudase alfa (XENPOZYME) is a sphingomyelin hydrolytic enzyme.

EMA: approved PMDA: approved Alimentary tract and metabolism (A16) A16AB25
Patents linked 0
Pipeline programs 1
News articles 0
Drug details — olipudase alfa
Class
Alimentary tract and metabolism (A16)
Route
Patents
0
Programs
1
Data quality
0.83

Quick answer

olipudase alfa (XENPOZYME) is a sphingomyelin hydrolytic enzyme.

Key facts

INN olipudase alfa
Brand XENPOZYME
Mechanism Sphingomyelin hydrolytic enzyme
Target Sphingomyelin
Therapeutic class Alimentary tract and metabolism (A16)
ATC code A16AB25

Mechanism of action

Sphingomyelin hydrolytic enzyme

Primary target: Sphingomyelin

Approval history

Authority Status Date
EMA approved
PMDA approved

Pipeline programs

  1. Xenpozyme (olipudase alfa,GZ402665) Phase 2 · Sanofi Winthrop Industrie · Niemann-Pick disease

Related & competitor drugs

  1. agalsidase alfa Alimentary tract and metabolism (A16)
  2. alogliptin Alimentary tract and metabolism (A10)
  3. alogliptin benzoate Alimentary tract and metabolism (A10)
  4. aprepitant Alimentary tract and metabolism (A04)
  5. budesonide Alimentary tract and metabolism (A07)
  6. canagliflozin Alimentary tract and metabolism (A10)

Frequently asked questions

What is olipudase alfa?

olipudase alfa (XENPOZYME) is a sphingomyelin hydrolytic enzyme.

What is the brand name for olipudase alfa?

XENPOZYME is a marketed brand name for olipudase alfa. Check FDA Drugs@FDA for the current US label holder and prescribing information.