Friday, July 10, 2026

Drug profile · INN

maralixibat

maralixibat (LIVMARLI) is a ileal bile acid transporter inhibitor.

EMA: application withdrawn Alimentary tract and metabolism (A05) A05AX
Patents linked 1
Pipeline programs 11
News articles 0
Drug details — maralixibat
Class
Alimentary tract and metabolism (A05)
Route
Patents
1
Programs
11
Data quality
0.83

Quick answer

maralixibat (LIVMARLI) is a ileal bile acid transporter inhibitor.

Key facts

INN maralixibat
Brand LIVMARLI
Mechanism Ileal bile acid transporter inhibitor
Target Ileal sodium/bile acid cotransporter
Therapeutic class Alimentary tract and metabolism (A05)
ATC code A05AX

Mechanism of action

Ileal bile acid transporter inhibitor

Primary target: Ileal sodium/bile acid cotransporter

Approval history

Authority Status Date
EMA application withdrawn

Pipeline programs

  1. MRX-802 Phase 3 · Anaxis Pharma · Cholestatic Pruritus
  2. Maralixibat Phase 3 · Mirum Pharmaceuticals International · Progressive Familial Intrahepatic Cholestasis (PFIC)
  3. Maralixibat Phase 3 · Mirum Pharmaceuticals International · Cholestatic Liver Disease (Except ALGS, PFIC, PBC and PSC)
  4. LUM001 (Maralixibat) Phase 2 · Mirum Pharmaceuticals International · Alagille Syndrome
  5. LUM001 (Maralixibat) Phase 2 · Mirum Pharmaceuticals International · Progressive Familial Intrahepatic Cholestasis (PFIC)
  6. Maralixibat Phase 2 · Mirum Pharmaceuticals International · Cholestatic Liver Disease
  7. Maralixibat Phase 2 · Mirum Pharmaceuticals International · Biliary Atresia
  8. Maralixibat Phase 2 · Mirum Pharmaceuticals International · Intrahepatic Cholestasis of Pregnancy

Related & competitor drugs

  1. agalsidase alfa Alimentary tract and metabolism (A16)
  2. alogliptin Alimentary tract and metabolism (A10)
  3. alogliptin benzoate Alimentary tract and metabolism (A10)
  4. aprepitant Alimentary tract and metabolism (A04)
  5. budesonide Alimentary tract and metabolism (A07)
  6. canagliflozin Alimentary tract and metabolism (A10)

Related patents

  1. US 12296050

    Pharmaceutical compositions comprising maralixibat and uses thereof

    Expires Mon May 08 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

Frequently asked questions

What is maralixibat?

maralixibat (LIVMARLI) is a ileal bile acid transporter inhibitor.

What is the brand name for maralixibat?

LIVMARLI is a marketed brand name for maralixibat. Check FDA Drugs@FDA for the current US label holder and prescribing information.