Friday, July 10, 2026

Drug profile · INN

iptacopan

iptacopan (FABHALTA) is a complement factor b inhibitor. Associated with Novartis Pharmaceuticals.

EMA: approved TGA: approved Antineoplastic and immunomodulating agents (L04) L04A
Patents linked 0
Pipeline programs 15
News articles 0
Drug details — iptacopan
Class
Antineoplastic and immunomodulating agents (L04)
Route
Patents
0
Programs
15
Data quality
0.83

Quick answer

iptacopan (FABHALTA) is a complement factor b inhibitor. Associated with Novartis Pharmaceuticals.

Key facts

INN iptacopan
Brand FABHALTA
Mechanism Complement factor B inhibitor
Target Complement factor B
Therapeutic class Antineoplastic and immunomodulating agents (L04)
ATC code L04A

Mechanism of action

Complement factor B inhibitor

Primary target: Complement factor B

Approval history

Authority Status Date
EMA approved
TGA approved

Pipeline programs

  1. CLNP023A2301 Phase 3 · Novartis India · IgA Nephropathy
  2. CLNP023B12301 Phase 3 · Novartis India · complement 3 glomerulopathy
  3. CLNP023Q12301 Phase 3 · Novartis India · generalized Myasthenia Gravis
  4. IPTACOPAN Phase 3 · Novartis India · Atypical Hemolytic Uremic Syndrome (aHUS)
  5. IPTACOPAN Phase 3 · Novartis India · Atypical Hemolytic Uremic Syndrome (aHUS)
  6. IPTACOPAN Phase 3 · Novartis India · Atypical hemolytic uremic syndrome
  7. IPTACOPAN HYDROCHLORIDE Phase 3 · Novartis India · Paroxysmal Nocturnal Hemoglobinuria (PNH)
  8. IPTACOPAN, LNP023 Phase 3 · Novartis India · Paroxysmal Nocturnal Hemoglobinuria (PNH)

Related & competitor drugs

  1. abiraterone acetate Antineoplastic and immunomodulating agents (L02)
  2. anagrelide Antineoplastic and immunomodulating agents (L01)
  3. apremilast Antineoplastic and immunomodulating agents (L04)
  4. arsenic trioxide Antineoplastic and immunomodulating agents (L01)
  5. axitinib Antineoplastic and immunomodulating agents (L01)
  6. azacitidine Antineoplastic and immunomodulating agents (L01)

Frequently asked questions

What is iptacopan?

iptacopan (FABHALTA) is a complement factor b inhibitor. Associated with Novartis Pharmaceuticals.

What is the brand name for iptacopan?

FABHALTA is a marketed brand name for iptacopan. Check FDA Drugs@FDA for the current US label holder and prescribing information.