Saturday, July 11, 2026

Drug profile · INN

etranacogene dezaparvovec

etranacogene dezaparvovec (HEMGENIX) is a coagulation factor ix exogenous protein.

EMA: approved Blood and blood forming organs (B02) B02BD
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Drug details — etranacogene dezaparvovec
Class
Blood and blood forming organs (B02)
Route
Patents
0
Programs
0
Data quality
0.83

Quick answer

etranacogene dezaparvovec (HEMGENIX) is a coagulation factor ix exogenous protein.

Key facts

INN etranacogene dezaparvovec
Brand HEMGENIX
Mechanism Coagulation factor IX exogenous protein
Target Coagulation factor IX
Therapeutic class Blood and blood forming organs (B02)
ATC code B02BD

Mechanism of action

Coagulation factor IX exogenous protein

Primary target: Coagulation factor IX

Approval history

Authority Status Date
EMA approved

Recent coverage

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Frequently asked questions

What is etranacogene dezaparvovec?

etranacogene dezaparvovec (HEMGENIX) is a coagulation factor ix exogenous protein.

What is the brand name for etranacogene dezaparvovec?

HEMGENIX is a marketed brand name for etranacogene dezaparvovec. Check FDA Drugs@FDA for the current US label holder and prescribing information.