Friday, July 10, 2026

Drug profile · INN

eladocagene exuparvovec

eladocagene exuparvovec (UPSTAZA) is a ddc exogenous gene.

EMA: approved Alimentary tract and metabolism (A16) A16AB26
Patents linked 0
Pipeline programs 2
News articles 0
Drug details — eladocagene exuparvovec
Class
Alimentary tract and metabolism (A16)
Route
Patents
0
Programs
2
Data quality
0.83

Quick answer

eladocagene exuparvovec (UPSTAZA) is a ddc exogenous gene.

Key facts

INN eladocagene exuparvovec
Brand UPSTAZA
Mechanism DDC exogenous gene
Target DDC
Therapeutic class Alimentary tract and metabolism (A16)
ATC code A16AB26

Mechanism of action

DDC exogenous gene

Primary target: DDC

Approval history

Authority Status Date
EMA approved

Pipeline programs

  1. AAV2-hAADC Phase 2 · PTC THERAPEUTICS · Aromatic Amino Acid Decarboxylase Deficiency
  2. Eladocagene Exuparvovec Phase 2 · PTC THERAPEUTICS · AADC Deficiency

Related & competitor drugs

  1. agalsidase alfa Alimentary tract and metabolism (A16)
  2. alogliptin Alimentary tract and metabolism (A10)
  3. alogliptin benzoate Alimentary tract and metabolism (A10)
  4. aprepitant Alimentary tract and metabolism (A04)
  5. budesonide Alimentary tract and metabolism (A07)
  6. canagliflozin Alimentary tract and metabolism (A10)

Frequently asked questions

What is eladocagene exuparvovec?

eladocagene exuparvovec (UPSTAZA) is a ddc exogenous gene.

What is the brand name for eladocagene exuparvovec?

UPSTAZA is a marketed brand name for eladocagene exuparvovec. Check FDA Drugs@FDA for the current US label holder and prescribing information.