Saturday, July 11, 2026

EMA · European Union

busulfan — EMA regulatory status

busulfan (MYLERAN) regulatory status in the European Union is tracked from public EMA records and cross-linked clinical and patent datasets on NovaPharmaNews. Current status: EMA approved.

Status snapshot

Status
EMA approved
Brand
MYLERAN
Mechanism
DNA inhibitor
Target
DNA
Structured fields
8

Sponsor / originator context: Lacuna Pharma Pty Ltd. Pipeline programs and exclusivity signals below are joined from ClinicalTrials.gov-linked projects and USPTO/EPO patent rows associated with this INN.

Pharmacology context used for competitive intelligence: DNA inhibitor. Target: DNA. This page is a status aggregation for professional reference — not prescribing advice.

Regional decision snapshot — EMA: approved.

Linked evidence on this spoke: 21 published clinical programs and 12 related patent records. Use the tables below for NCT identifiers, phases, and exclusivity dates; verify against primary sources before BD or medical decisions.

Regulatory timeline

Regulator Region Status Date Source
EMA European Union approved Evidence

Linked clinical programs

Program Phase Sponsor NCT
2019/2894 Phase 3 George Institute for 2024-514917-36-00
ALL SCTped FORUM Phase 3 George Institute for 2024-512657-24-00
Busulfan (BU) Phase 3 First People's Hospital NCT03733327
CTX001-111 Phase 3 Vertex Pharmaceuticals (Australia) 2024-516894-57-00
DAUNORUBICIN for Favorable-intermediate-risk Acu… Phase 3 Telethon Foundation 2023-510433-29-00
FEDR-MF-002 Phase 3 Celgene 2024-511972-33-00
MDS0519 Phase 3 Telethon Foundation 2023-510515-19-00
MK-3543-006 Phase 3 MSD Merck Sharp 2023-504865-21-00
OTL-103-4 Phase 3 Telethon Foundation 2024-517792-20-00
OTL-203-02 Phase 3 ORCHARD THERAPEUTICS 2022-500306-17-00
VX21-CTX001-141 Phase 3 Vertex Pharmaceuticals (Australia) 2024-513349-35-00
VX21-CTX001-151 Phase 3 Vertex Pharmaceuticals (Australia) 2024-513978-22-00

Related patents

Number Title Jurisdiction
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11827900 Engineered target specific nucleases US
11793888 Methods and compositions for engineering immunity US
11723952 Methods and compositions for treating Huntington's Disease US
11690921 Delivery of target specific nucleases US
11661612 DNA-binding proteins and uses thereof US
11661611 Genetic modification of cytokine inducible SH2-containing protein (CISH) gene US

Related hubs

FAQ

What is the EMA approval status of busulfan?

busulfan currently shows EMA approved in our European Union regulatory index. Confirm on the official EMA label or EPAR before clinical or commercial use.

Where does NovaPharmaNews get busulfan regulatory data?

Status fields are joined from public sources (openFDA / EMA / regional agencies), ClinicalTrials.gov-linked programs, and patent registries. See /about/data-sources for attribution.

How many clinical programs are linked to busulfan?

This spoke lists 21 published programs associated with busulfan in our pipeline index.