🇺🇸 FDA
Pipeline program

Sodium phenylbutyrate

STUDY24100064

Phase 2 small_molecule active

Quick answer

Sodium phenylbutyrate for Medium-chain Acyl-CoA Dehydrogenase Deficiency is a Phase 2 program (small_molecule) at ZEVRA THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
ZEVRA THERAPEUTICS, INC.
Indication
Medium-chain Acyl-CoA Dehydrogenase Deficiency
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials