🇺🇸 FDA
Pipeline program

4-aminopyridine

AAAI7400

Phase 3 small_molecule completed

Quick answer

4-aminopyridine for Spinal Muscular Atrophy is a Phase 3 program (small_molecule) at UNITED THERAPEUTICS Corp with 1 ClinicalTrials.gov record(s).

Program details

Company
UNITED THERAPEUTICS Corp
Indication
Spinal Muscular Atrophy
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials