🇺🇸 FDA
Pipeline program

UX016

UX016-CL210

Phase 2 small_molecule active

Quick answer

UX016 for GNE Myopathy is a Phase 2 program (small_molecule) at Ultragenyx UK Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx UK Limited
Indication
GNE Myopathy
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials