pharma · Cystic Fibrosis · Multiple Sclerosis · RARE
Ultragenyx UK
Ultragenyx UK Limited
UGenDx is a pharma organization headquartered in NOVATO, CA, GB. It trades on NYSE under ticker RARE. Primary therapeutic focus areas include Cystic Fibrosis, Multiple Sclerosis, Fanconi's Anemia, Hereditary Inclusion Bo
Company details
- Status
- Public
- HQ
- Newcastle upon tyne, NE128RL, GB, NOVATO, CA
- Founded
- 2024
- Employees
- 2
- Programs
- 201
- Drugs
- 168
- Patents
- 23
Intrathecal recombinant human alpha iduronidase
Unknown · small molecule · Mucopolysaccharidosis I
Intrathecal recombinant human alpha iduronidase for Mucopolysaccharidosis I is a Unknown program (small_molecule) at Ultragenyx UK Limited with 1 ClinicalTrials.gov record(s).
Internal code MIRC-002 (100)
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- Ultragenyx UK Limited
- Phase
- Unknown
- Modality
- small_molecule
- Indication
- Mucopolysaccharidosis I
- Status
- terminated
- Trials
- 1