🇺🇸 FDA
Pipeline program

Intrathecal recombinant human alpha iduronidase

MIRC-002 (100)

Unknown small_molecule terminated

Quick answer

Intrathecal recombinant human alpha iduronidase for Mucopolysaccharidosis I is a Unknown program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Mucopolysaccharidosis I
Phase
Unknown
Modality
small_molecule
Status
terminated

Clinical trials