DTX301
DTX301-CL301
Phase 3 gene_therapy active
Quick answer
DTX301 for OTC Deficiency is a Phase 3 program (gene_therapy) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Ultragenyx Pharmaceutical
- Indication
- OTC Deficiency
- Phase
- Phase 3
- Modality
- gene_therapy
- Status
- active