Ambroxol Hydrochloride 30 mg tablet - 9 mg/kg/day
24-LDRTC-01
Phase 3 small_molecule active
Quick answer
Ambroxol Hydrochloride 30 mg tablet - 9 mg/kg/day for Sanfilippo Syndrome is a Phase 3 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Ultragenyx Pharmaceutical
- Indication
- Sanfilippo Syndrome
- Phase
- Phase 3
- Modality
- small_molecule
- Status
- active