🇺🇸 FDA
Pipeline program

Aceneuramic Acid Extended-Release Tablets

UX001-CL302

Phase 3 small_molecule terminated

Quick answer

Aceneuramic Acid Extended-Release Tablets for Hereditary Inclusion Body Myopathy is a Phase 3 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Hereditary Inclusion Body Myopathy
Phase
Phase 3
Modality
small_molecule
Status
terminated

Clinical trials