Friday, July 10, 2026

pharma · Metachromatic Leukodystrophy (MLD) · Late Metachromatic Leukodystrophy (MLD)

Shire

Shire is a pharma organization headquartered in CN. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Late Metachromatic Leukodystrophy (MLD), Hunter Syndrome, Cytomegalovirus (CMV), Crohn's Dis

JP HQ
3,523 Employees
NMPA registrant Type
Company details
Status
Public
HQ
JP
Employees
3,523
Programs
9
Drugs
8
Patents
0
Clinical program

rhASA

Phase 2 · small molecule · Late Metachromatic Leukodystrophy (MLD)

rhASA for Late Metachromatic Leukodystrophy (MLD) is a Phase 2 program (small_molecule) at Shire with 1 ClinicalTrials.gov record(s).

← All Shire projects Phase 2 small molecule active

Internal code SHP611-201

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Shire
Phase
Phase 2
Modality
small_molecule
Indication
Late Metachromatic Leukodystrophy (MLD)
Status
active
Trials
1

Clinical trials