🇺🇸 FDA
Pipeline program

Cemdisiran

R3918-PNH-2022

Phase 3 small_molecule terminated

Quick answer

Cemdisiran for Paroxysmal Nocturnal Hemoglobinuria is a Phase 3 program (small_molecule) at REGENERON PHARMACEUTICALS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
REGENERON PHARMACEUTICALS, INC.
Indication
Paroxysmal Nocturnal Hemoglobinuria
Phase
Phase 3
Modality
small_molecule
Status
terminated

Clinical trials