pharma · Cholestatic liver disease · Cystic Fibrosis · PRQR
ProQR Therapeutics N.V
ProQR Therapeutics N.V.
ProQR Therapeutics is a pharma organization headquartered in Leiden, NL. It trades on NYSE under ticker PRQR. Primary therapeutic focus areas include Cholestatic liver disease, Cystic Fibrosis, Autosomal Dominant Retinit
Company details
- Status
- Public
- HQ
- Leiden, NL
- Founded
- 2012
- Employees
- 204
- Programs
- 6
- Drugs
- 2
- Patents
- 19
sepofarsen
Phase 3 · small molecule · Leber Congenital Amaurosis 10
sepofarsen for Leber Congenital Amaurosis 10 is a Phase 3 program (small_molecule) at ProQR Therapeutics N.V. with 2 ClinicalTrials.gov record(s).
Internal code PQ-110-003
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- ProQR Therapeutics N.V.
- Phase
- Phase 3
- Modality
- small_molecule
- Indication
- Leber Congenital Amaurosis 10
- Status
- active
- Trials
- 2