🇺🇸 FDA
Pipeline program

PLX-200

PLX-200-002

Phase 3 small_molecule active

Quick answer

PLX-200 for Juvenile Neuronal Ceroid Lipofuscinosis is a Phase 3 program (small_molecule) at Polaryx Therapeutics with 1 ClinicalTrials.gov record(s).

Program details

Company
Polaryx Therapeutics
Indication
Juvenile Neuronal Ceroid Lipofuscinosis
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials