🇺🇸 FDA
Pipeline program

Pozelimab, Cemdisiran

R3918-PNH-2483

Phase 3 small_molecule active

Quick answer

Pozelimab, Cemdisiran for Paroxysmal nocturnal hemoglobinuria (PNH) is a Phase 3 program (small_molecule) at Pharma Mar S.A. with 1 ClinicalTrials.gov record(s).

Program details

Company
Pharma Mar S.A.
Indication
Paroxysmal nocturnal hemoglobinuria (PNH)
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials