🇺🇸 FDA
Pipeline program

Prednisolon STADA® 5 mg Tabletten, Prednisolone placebo hard capsule, 10 mg, Prednisolone Placebo hard capsule, 5mg, Prednisolon STADA® 10 mg Tabletten, Pariglasgene brecaparvovec, Normal Saline

DTX401-CL301

Phase 3 small_molecule active

Quick answer

Prednisolon STADA® 5 mg Tabletten, Prednisolone placebo hard capsule, 10 mg, Prednisolone Placebo hard capsule, 5mg, Prednisolon STADA® 10 mg Tabletten, Pariglasgene brecaparvovec, Normal Saline for Glycogen Storage Disease Type Ia (GSDIa) is a Phase 3 program (small_molecule) at Pharma Mar S.A. with 1 ClinicalTrials.gov record(s).

Program details

Company
Pharma Mar S.A.
Indication
Glycogen Storage Disease Type Ia (GSDIa)
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials