🇺🇸 FDA
Pipeline program

Prednisolon STADA® 5 mg Tabletten, Prednisolone placebo hard capsule and tablet, Normal Saline, Prednisolon STADA® 10 mg Tabletten, [1-13C]SODIUM ACETATE, Avalotcagene ontaparvovec

DTX301-CL301

Phase 3 small_molecule active

Quick answer

Prednisolon STADA® 5 mg Tabletten, Prednisolone placebo hard capsule and tablet, Normal Saline, Prednisolon STADA® 10 mg Tabletten, [1-13C]SODIUM ACETATE, Avalotcagene ontaparvovec for Late-onset Ornithine transcarbamylase (OTC) deficiency is a Phase 3 program (small_molecule) at Pharma Mar S.A. with 1 ClinicalTrials.gov record(s).

Program details

Company
Pharma Mar S.A.
Indication
Late-onset Ornithine transcarbamylase (OTC) deficiency
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials