🇺🇸 FDA
Pipeline program

RAVICTI 1.1 g/ml oral liquid

APHP230834

Phase 2 small_molecule active

Quick answer

RAVICTI 1.1 g/ml oral liquid for Pyruvate dehydrogenase deficiency is a Phase 2 program (small_molecule) at Pari Pharma GmbH with 1 ClinicalTrials.gov record(s).

Program details

Company
Pari Pharma GmbH
Indication
Pyruvate dehydrogenase deficiency
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials