🇺🇸 FDA
Pipeline program

AN OPEN-LABEL, MULTICENTER STUDY IN MALE PEDIATRIC PATIENTS WITH CEREBRAL X-LINKED ADRENOLEUKODYSTROPHY (CALD) TO ASSESS THE EFFECTS OF MIN-102 TREATMENT ON DISEASE PROGRESSION PRIOR TO HUMAN STEM CELL TRANSPLANT (HSCT)

MT-2-02

Phase 2 other active

Quick answer

AN OPEN-LABEL, MULTICENTER STUDY IN MALE PEDIATRIC PATIENTS WITH CEREBRAL X-LINKED ADRENOLEUKODYSTROPHY (CALD) TO ASSESS THE EFFECTS OF MIN-102 TREATMENT ON DISEASE PROGRESSION PRIOR TO HUMAN STEM CELL TRANSPLANT (HSCT) for CEREBRAL X-LINKED ADRENOLEUKODYSTROPHY (CALD) is a Phase 2 program (other) at Minoryx Therapeutics S.L. with 1 ClinicalTrials.gov record(s).

Program details

Company
Minoryx Therapeutics S.L.
Indication
CEREBRAL X-LINKED ADRENOLEUKODYSTROPHY (CALD)
Phase
Phase 2
Modality
other
Status
active

Clinical trials