Company profile · Sponsor
Larimar
Larimar Therapeutics
- Pipeline
- 3
- Drugs
- 0
- Patents
- 5
Quick answer
Larimar (LRMR) is a pharma company. headquartered in BALA CYNWYD, PA, USA. listed on NYSE. NovaPharmaNews links 3 pipeline programs, 0 drugs, and 5 patents to this profile..
Company facts
Pipeline (3)
Search pipeline →-
Nomlabofusp, Placebo to Nomlabofusp
Larimar
Friedreich’s ataxia is the most common inherited ataxia in humans and results from a deficiency of the mitochondrial protein, FXN. Friedreich’s ataxia is a rare, progressive, multisystem disease with an incidence that is estimated to be 1:29,000, and a carrier frequency of ~1:85.
1 trial -
CTI-1601
Larimar
Friedreich Ataxia
4 trials -
Nomlabofusp
Larimar
Friedreich Ataxia
1 trial
Patents (5)
Search patents →-
US 12390509
Pharmaceutical composition comprising frataxin fusion protein and methods of use thereof
granted -
US 12351611
Molecules for organelle-specific protein delivery
granted -
US 12091437
Molecules for organelle-specific protein delivery
granted -
US 11976100
Methods for treating myelin associated diseases and mitochondria associated diseases
granted -
US 11891420
Molecules for organelle-specific protein delivery
granted
Frequently asked questions
What is Larimar?
Larimar (LRMR) is a pharma company. headquartered in BALA CYNWYD, PA, USA. listed on NYSE. NovaPharmaNews links 3 pipeline programs, 0 drugs, and 5 patents to this profile..
What pipeline programs does Larimar sponsor?
We track 3 ClinicalTrials.gov-linked programs for Larimar, including Nomlabofusp, Placebo to Nomlabofusp and 2 more. Open each program for phase, modality, NCT IDs, and indication details.
Where does Larimar company data come from?
Profiles combine SEC EDGAR (CIK/ticker), ClinicalTrials.gov sponsor links, FDA drug records, and USPTO patent metadata. See our data sources page. This profile is for professional reference, not investment advice.