🇺🇸 FDA
Pipeline program

Tofersen

233AS102

Phase 3 small_molecule completed

Quick answer

Tofersen for ALS Caused by Superoxide Dismutase 1 (SOD1) Mutation is a Phase 3 program (small_molecule) at IONIS PHARMACEUTICALS INC with 1 ClinicalTrials.gov record(s).

Program details

Company
IONIS PHARMACEUTICALS INC
Indication
ALS Caused by Superoxide Dismutase 1 (SOD1) Mutation
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials