🇺🇸 FDA
Pipeline program

IONIS-DMPKRx

ISIS 598769-CS2

Phase 2 small_molecule completed

Quick answer

IONIS-DMPKRx for Myotonic Dystrophy Type 1 is a Phase 2 program (small_molecule) at IONIS PHARMACEUTICALS INC with 1 ClinicalTrials.gov record(s).

Program details

Company
IONIS PHARMACEUTICALS INC
Indication
Myotonic Dystrophy Type 1
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials