🇺🇸 FDA
Pipeline program

ION582

ION582-CS2

Phase 3 small_molecule active

Quick answer

ION582 for Angelman Syndrome is a Phase 3 program (small_molecule) at IONIS PHARMACEUTICALS INC with 2 ClinicalTrials.gov record(s).

Program details

Company
IONIS PHARMACEUTICALS INC
Indication
Angelman Syndrome
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials