🇺🇸 FDA
Pipeline program

ION356

ION356-CS1

Phase 1 small_molecule active

Quick answer

ION356 for Pelizaeus-Merzbacher Disease is a Phase 1 program (small_molecule) at IONIS PHARMACEUTICALS INC with 1 ClinicalTrials.gov record(s).

Program details

Company
IONIS PHARMACEUTICALS INC
Indication
Pelizaeus-Merzbacher Disease
Phase
Phase 1
Modality
small_molecule
Status
active

Clinical trials