Wednesday, June 10, 2026

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IONIS PHARMACEUTICALS

IONIS PHARMACEUTICALS drug portfolio β€” 48 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

2855 Gazelle Ct, Carlsbad, CA 92010, US HQ
1989 Founded
1,493 Employees
Public company Type
IONS Β· NYSE Ticker
Company details
Status
Public
HQ
2855 Gazelle Ct, Carlsbad, CA 92010, US
Founded
1989
Employees
1,493
Programs
128
Drugs
48
Patents
222
Intelligence Β· Drug Pipeline

IONIS PHARMACEUTICALS pipeline

Portfolio lens on 48 drugs and development assets β€” regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

IONIS PHARMACEUTICALS drug portfolio β€” 48 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

48 compounds
  1. US regulatory status: approved. Molecular target: Human immunodeficiency virus type 1 reverse transcriptase.

    Target
    Human immunodeficiency virus type 1 reverse transcriptase
    Mechanism
    Human immunodeficiency virus type 1 reverse transcriptase inhibitor
  2. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  3. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  4. US regulatory status: approved.

  5. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  6. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  7. asenapine

    Nervous system (N05)

    US regulatory status: approved. Mechanism: Serotonin 2a (5-HT2a) receptor antagonist.

    Mechanism
    Serotonin 2a (5-HT2a) receptor antagonist
  8. US regulatory status: approved. Mechanism: Dihydrofolate reductase inhibitor.

    Mechanism
    Dihydrofolate reductase inhibitor
  9. US regulatory status: approved. Molecular target: Sodium channel alpha subunit.

    Target
    Sodium channel alpha subunit
    Mechanism
    Sodium channel alpha subunit blocker
  10. US regulatory status: approved. Mechanism: Unknown.

    Mechanism
    Unknown
  11. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  12. donidalorsen

    Blood and blood forming organs (B06)

    Blood and blood forming organs (B06) compound in IONIS PHARMACEUTICALS's portfolio.

  13. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  14. eplontersen

    Nervous system (N07)

    Nervous system (N07) compound in IONIS PHARMACEUTICALS's portfolio. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin antisense inhibitor
  15. US regulatory status: approved. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA antisense inhibitor
  16. US regulatory status: approved. Molecular target: Estrogen receptor.

    Target
    Estrogen receptor
    Mechanism
    Estrogen receptor alpha agonist
  17. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  18. fomivirsen

    Sensory organs (S01)

    Sensory organs (S01) compound in IONIS PHARMACEUTICALS's portfolio. Molecular target: Major intermediate early region 2 mRNA.

    Target
    Major intermediate early region 2 mRNA
    Mechanism
    Major intermediate early region 2 mRNA antisense inhibitor
  19. US regulatory status: approved. Molecular target: Major intermediate early region 2 mRNA.

    Target
    Major intermediate early region 2 mRNA
    Mechanism
    Major intermediate early region 2 mRNA antisense inhibitor
  20. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  21. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  22. inotersen

    Nervous system (N07)

    Nervous system (N07) compound in IONIS PHARMACEUTICALS's portfolio. Mechanism: Transthyretin ANTISENSE inhibitor.

    Mechanism
    Transthyretin ANTISENSE inhibitor
  23. US regulatory status: approved. Molecular target: Transthyretin mRNA.

    Target
    Transthyretin mRNA
    Mechanism
    Transthyretin mRNA antisense inhibitor
  24. US regulatory status: approved. Molecular target: Cyclooxygenase.

    Target
    Cyclooxygenase
    Mechanism
    Cyclooxygenase inhibitor
  25. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  26. mipomersen sodium

    Cardiovascular system (C10)

    US regulatory status: approved. Molecular target: Apo-B 100 mRNA.

    Target
    Apo-B 100 mRNA
    Mechanism
    Apo-B 100 mRNA antisense inhibitor
  27. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  28. olezarsen

    Cardiovascular system (C10)

    Cardiovascular system (C10) compound in IONIS PHARMACEUTICALS's portfolio. Molecular target: Apolipoprotein C-III mRNA.

    Target
    Apolipoprotein C-III mRNA
    Mechanism
    Apolipoprotein C-III mRNA antisense inhibitor
  29. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  30. US regulatory status: approved. Molecular target: Copper.

    Target
    Copper
    Mechanism
    Copper chelating agent
  31. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  32. ribavirin

    Antiinfectives for systemic use (J05)

    US regulatory status: approved. Molecular target: Inosine-5'-monophosphate dehydrogenase 1.

    Target
    Inosine-5'-monophosphate dehydrogenase 1
    Mechanism
    Inosine-5'-monophosphate dehydrogenase 1 inhibitor
  33. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  34. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  35. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  36. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records.

  37. tofersen

    Nervous system (N07)

    US regulatory status: approved. Molecular target: SOD1 mRNA.

    Target
    SOD1 mRNA
    Mechanism
    SOD1 mRNA inhibitor
  38. volanesorsen

    Cardiovascular system (C10)

    Cardiovascular system (C10) compound in IONIS PHARMACEUTICALS's portfolio. Mechanism: Apolipoprotein C-III mRNA 3'UTR antisense inhibitor.

    Mechanism
    Apolipoprotein C-III mRNA 3'UTR antisense inhibitor
  39. Development asset linked to IONIS PHARMACEUTICALS in public FDA and regional records. Mechanism: Vitamin k epoxide reductase complex subunit 1 isoform 1 inhibitor.

    Mechanism
    Vitamin k epoxide reductase complex subunit 1 isoform 1 inhibitor
  40. US regulatory status: approved. Molecular target: Vitamin K epoxide reductase complex subunit 1.

    Target
    Vitamin K epoxide reductase complex subunit 1
    Mechanism
    Vitamin k epoxide reductase complex subunit 1 isoform 1 inhibitor