🇺🇸 FDA
Pipeline program

Granules for oral suspension, N-Acetyl-L-Leucine

IB1001-301

Phase 3 small_molecule active

Quick answer

Granules for oral suspension, N-Acetyl-L-Leucine for Niemann-Pick disease type C is a Phase 3 program (small_molecule) at Intrabio Ireland Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
Intrabio Ireland Limited
Indication
Niemann-Pick disease type C
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials