🇺🇸 FDA
Pipeline program

Myozyme 50 mg powder for concentrate for solution for infusion

Pompe phys 02

Approved small_molecule active

Quick answer

Myozyme 50 mg powder for concentrate for solution for infusion for Pompe disease / glycogenosis type II / acid maltase deficiency is a Approved program (small_molecule) at Disc Medicine with 1 ClinicalTrials.gov record(s).

Program details

Company
Disc Medicine
Indication
Pompe disease / glycogenosis type II / acid maltase deficiency
Phase
Approved
Modality
small_molecule
Status
active

Clinical trials