🇺🇸 FDA
Pipeline program

Myozyme 50 mg powder for concentrate for solution for infusion, Opfolda 65 mg hard capsules, Pombiliti 105 mg powder for concentrate for solution for infusion, Nexviadyme 100 mg powder for concentrate for solution for infusion

Approved small_molecule active

Quick answer

Myozyme 50 mg powder for concentrate for solution for infusion, Opfolda 65 mg hard capsules, Pombiliti 105 mg powder for concentrate for solution for infusion, Nexviadyme 100 mg powder for concentrate for solution for infusion for Pompe disease is a Approved program (small_molecule) at Disc Medicine with 1 ClinicalTrials.gov record(s).

Program details

Company
Disc Medicine
Indication
Pompe disease
Phase
Approved
Modality
small_molecule
Status
active

Clinical trials