🇺🇸 FDA
Pipeline program

Ultomiris 300 mg/30 mL concentrate for solution for infusion

116326

Approved small_molecule active

Quick answer

Ultomiris 300 mg/30 mL concentrate for solution for infusion for Paroxysmal nocturnal hemoglobinuria (PNH) is a Approved program (small_molecule) at Disc Medicine with 1 ClinicalTrials.gov record(s).

Program details

Company
Disc Medicine
Indication
Paroxysmal nocturnal hemoglobinuria (PNH)
Phase
Approved
Modality
small_molecule
Status
active

Clinical trials