🇺🇸 FDA
Pipeline program

DT-216P2

DTX-216P2-011

Phase 2 small_molecule active

Quick answer

DT-216P2 for Friedreich Ataxia is a Phase 2 program (small_molecule) at Design Therapeutics with 2 ClinicalTrials.gov record(s).

Program details

Company
Design Therapeutics
Indication
Friedreich Ataxia
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials