🇺🇸 FDA
Pipeline program

DT-216

DTX-216-102

Phase 1 small_molecule completed

Quick answer

DT-216 for Friedreich Ataxia is a Phase 1 program (small_molecule) at Design Therapeutics with 2 ClinicalTrials.gov record(s).

Program details

Company
Design Therapeutics
Indication
Friedreich Ataxia
Phase
Phase 1
Modality
small_molecule
Status
completed

Clinical trials