Glycerol Phenylbutyrate 1100 MG/ML [Ravicti]
19-10020997
Phase 1 small_molecule active
Quick answer
Glycerol Phenylbutyrate 1100 MG/ML [Ravicti] for STXBP1 Encephalopathy With Epilepsy, SLC6A1 Neurodevelopmental Disorder is a Phase 1 program (small_molecule) at Connect Biopharma Holdings Ltd with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Connect Biopharma Holdings Ltd
- Indication
- STXBP1 Encephalopathy With Epilepsy, SLC6A1 Neurodevelopmental Disorder
- Phase
- Phase 1
- Modality
- small_molecule
- Status
- active